The increasing incidence of genetic and rare diseases is a major factor driving revenue growth in the Antisense ...

UCB’s continued commitment to leading research aimed at improving treatment outcomes for people living with neurological conditions.Data include the use of FINTEPLA®▼ (fenfluramine)1 in Dravet ...

Describes the nature of a clinical study. Types include: Observational study — observes people and measures outcomes without affecting results. Interventional study (clinical trial) — studies new ...

While Harmony Biosciences HRMY may not be a typical cannabis stock involved in cultivation, processing, or sales of marijuana ...

Nosological limits Unlike epilepsy syndromes for which clinical manifestations are closely tied to a specific genetic cause, such as Dravet syndrome or CDKL5 -related developmental epileptic ...